RNA Revolution: Advancing Drug Discovery through Targeted Molecules

https://www.pharmafocusamerica.com/articles/rna-revolution-advancing-drug-discovery-through-targeted-molecules

The RNA revolution in drug discovery has introduced targeted molecules like ASOs, siRNA, and RNA vaccines, offering precise gene modulation and therapeutic versatility across genetic disorders, neurodegenerative diseases, infectious diseases, and cancer. Challenges include delivery efficiency and immunogenicity, driving research toward innovative solutions for future healthcare advancements.